Treatment

0.9% Sodium Chloride Injection, mRNA-3705 clinical trials

1 indexed studies · 0 currently recruiting

Ongoing, recruitingPhase I and Phase II (Integrated)- First administration to humans
A Global, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacodynamics, and Pharmacokinetics of mRNA-3705 in Participants with Isolated Methylmalonic Acidemia Due to Methylmalonyl-CoA Mutase Deficiency
This study is testing a new medicine, mRNA-3705, for a rare genetic condition called methylmalonic acidemia (MMA). Doctors want to see if the medicine is safe, how the body handles it, and if it helps reduce harmful acid levels in the blood.
For: Isolated Methylmalonic Acidemia Due to Methylmalonyl-CoA Mutase Deficiency
France · Netherlands · Spain