APL-3007 clinical trials

Safety and tolerability of APL-3007 administered as a single dose in addition to background therapy with a C5 inhibitor in adults with paroxysmal nocturnal hemoglobinuria

This study is testing a new medicine, APL-3007, for adults with a rare blood condition called PNH. We want to see how safe it is and if people can take it well alongside their usual PNH treatment. It's an early-stage study to gather important safety information.