Calculation of the metabolic balance score clinical trials

Evaluation of Therapeutic Adherence Among Patients Followed in the Department of Hereditary Metabolic Diseases at Necker Hospital

This study at Necker Hospital looks at how well people with inherited metabolic diseases take their daily medicines. We want to see if a special workshop is needed to help patients and their families manage their medication better. It includes children from 7 years old to young adults up to 20.