All treatments
Treatment
Cardiac evaluation clinical trials
2 indexed studies · 2 currently recruiting
- Recruiting
Natural History Study of Children With LAMA2-related Dystrophies
This study looks at how a rare muscle condition called LAMA2-related dystrophy affects children in France. Researchers will follow children aged 2-15 for two years, checking their muscle strength, breathing, thinking skills, and overall well-being. The goal is to better understand the condition and prepare for future treatments.
For: Merosin Deficient Congenital Muscular DystrophyFrance - RecruitingNA
Characterization of New Phenotypes of Patients With Spinal Muscular Atrophy Treated With SMN Restoring Therapy
This study looks at children under 16 with Spinal Muscular Atrophy (SMA) who are receiving new treatments. We want to understand how these treatments are changing the disease and find the best ways to check on patients' health and progress.
For: Spinal Muscular AtrophyFrance