CSL222 (AAV5-hFIXco-Padua) clinical trials

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

This study looks at a gene therapy called CSL222 for adults with Hemophilia B. It specifically checks if the treatment helps reduce bleeding in people who already have certain natural antibodies to the gene therapy virus.