- Active not recruitingPHASE3
Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX
This study looks closely at a new medicine called fitusiran for men with haemophilia A or B. It aims to see how safe the medicine is over a long time and how well it prevents bleeding, as well as if it improves quality of life.
For: HemophiliaUnited States · Australia · Canada - RecruitingPHASE3
A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B
This study is testing a new medicine, Fitusiran, for boys aged 1 to 11 with severe haemophilia A or B. It aims to see how well it prevents bleeding and if it's safe. Some boys will receive Fitusiran for the first time, while others have already been taking it.
For: HemophiliaUnited States · Belgium · Brazil