- RecruitingPHASE3
A Gaucher Disease Gene Therapy Trial With FLT201
This study is testing a new gene therapy called FLT201 for adults with Gaucher disease type 1. It aims to see if patients can stop their current treatment after receiving FLT201 while remaining well. This is the final stage of testing before it might become available.
For: Gaucher Disease Type 1United States · Argentina · Australia - Active not recruitingPHASE1, PHASE2
Long Term Follow-up Study of Type-1 Gaucher Subjects Post FLT201 Dose (GALILEO-2)
This study is checking on the long-term health of people with Type 1 Gaucher disease who previously received a treatment called FLT201 in an earlier trial. We'll follow them for five years to see how they're doing.
For: Gaucher Disease, Type 1United States · Brazil · Spain