- RecruitingPHASE2
Rescue of Nephrons With ALE.F02 (RENAL-F02)
This study looks into a new drug, ALE.F02, to see if it can help protect kidneys in people with a condition called ANCA-associated vasculitis (AAV). Researchers want to check if it's safe and effective at preserving kidney function.
For: Glomerulonephritis Rapidly ProgressiveCzechia · Denmark · France - RecruitingPHASE3
A 52-week Study of Rilzabrutinib Efficacy and Safety Compared to Placebo in Adults Diagnosed With IgG4-related Disease
This study is looking into a new medication, rilzabrutinib, for adults with a condition called IgG4-related disease. It compares the medication to a dummy pill to see if it's safe and helps control the disease over 52 weeks.
For: Immunoglobulin G4 Related DiseaseUnited States · Argentina · Belgium - Active not recruitingPHASE3
A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4
This study is testing an experimental gene therapy, SRP-9003, for Limb-girdle Muscular Dystrophy type 2E/R4 (LGMD2E/R4). It aims to see how a single dose affects a specific gene in people who can walk and those who can't.
For: Limb-girdle Muscular DystrophyUnited States · Belgium · Germany