INZ-701, INZ-701 clinical trials

The ENERGY Study: An Open-Label Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of INZ-701 in Infants with Ectonucleotide Pyrophosphatase/ Phosphodiesterase 1 (ENPP1) Deficiency or ATP-binding Cassette Sub-family C Member 6 (ABCC6) Deficiency

This study, called ENERGY, is looking at a new medicine called INZ-701 for babies with certain rare genetic conditions. Doctors want to see if the medicine is safe, how it's handled by the body, and if it helps by checking things like blood and heart health.