NS-089/NCNP-02 clinical trials

NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

This study is testing a new medicine, NS-089/NCNP-02, for Duchenne muscular dystrophy (DMD) in boys aged 4 to 14. It's for those with a specific gene change (exon 44 skipping) and involves weekly IV infusions to see if the medicine is safe and helps their condition.