PBFT02 clinical trials

A Study of PBFT02 in Participants With FTD and Mutations in the Granulin Precursor (GRN) or C9ORF72 Genes

This study is testing a new gene therapy called PBFT02 for a type of dementia called Frontotemporal Dementia (FTD). It aims to see if PBFT02 is safe, well-tolerated, and can help people with FTD caused by specific gene problems (GRN or C9ORF72 mutations).