PTC857, Placebo to match PTC857 60 mg/mL oral solution, Utreloxastat 62.5 clinical trials

A Phase 2, Randomized, Double-Blind, Placebo-Controlled, Parallel Study to Assess the Efficacy, Safety, Tolerability, PK, and Biomarker Effects of PTC857 in Adult Subjects With Amyotrophic Lateral Sclerosis (CARDINALS)

This study is testing a new medicine, PTC857, for people with Amyotrophic Lateral Sclerosis (ALS), also known as Motor Neurone Disease. We want to see if it helps improve daily activities and how safe it is compared to a dummy medicine.