Study product: UK-PKAN-B5D (capsule containing 4ʹ-phosphopantetheine [4ʹ-PPT]) or matched placebo). To be dosed enterall clinical trials

Investigating 4’PPT for pantothenate kinase associated neurodegeneration (PKAN)

This study is testing a new form of vitamin B5 called UK-PKAN-B5D for a rare, severe brain condition called PKAN. It aims to see if this new treatment is safe and well-tolerated in young people aged 1 to 25.