This was a six-part, prospective, multicenter, multiregional, observational study designed to evaluate biomarkers and as clinical trials

A study of potential treatment-responsive biomarkers and clinical outcomes in Hunter syndrome

This study looked at how Hunter Syndrome affects people over time, including changes in behaviour, thinking abilities, and levels of certain signs in the body. It aimed to understand the condition better and find ways to measure if future treatments are working, without giving any new medicines.