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venglustat (GZ402671) clinical trials
3 indexed studies · 0 currently recruiting
- Active not recruitingPHASE2
Venglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy Extension
This study is looking at a new medication, venglustat, for adults with a rare genetic condition called Gaucher disease, specifically types 1 and 3. Researchers want to see if venglustat, alone or with another drug called Cerezyme, is safe and helps improve symptoms.
For: Gaucher Disease Type 1 · Gaucher Disease Type 3United States · Germany · Japan - Active not recruitingPHASE3
A Study to Evaluate the Effect of Venglustat Tablets on Left Ventricular Mass Index in Male and Female Adult Participants With Fabry Disease
This study looks at a new tablet treatment called venglustat for people with Fabry disease. It compares venglustat to usual treatments to see how it affects heart thickness in adults with Fabry disease.
For: Fabry DiseaseUnited States · Austria · Canada - Active not recruitingPHASE3
A Study to Evaluate the Effect of Venglustat Tablets on Neuropathic and Abdominal Pain in Male and Female Participants ≥16 Years of Age With Fabry Disease
This study is looking into whether a tablet called Venglustat can help reduce nerve pain and tummy pain in people aged 16 and over with Fabry disease. We want to see if it works better than a dummy tablet.
For: Fabry DiseaseUnited States · Argentina · Australia