Congenital Adrenal Hyperplasia research hub
9 indexed studies · 6 currently recruiting
- recruitingPHASE2, PHASE3
A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)
This study is looking into a new medication called atumelnant for children and teenagers with a condition called Congenital Adrenal Hyperplasia (CAH). It wants to see if the medication is safe, works well, and how the body handles it.
United States · Argentina · Australia - recruitingPHASE1, PHASE2
A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia
This study is looking into a new medicine called Lu AG13909 for adults with Congenital Adrenal Hyperplasia (CAH). It will check if the medicine is safe, how the body handles it, and how effective it is in different doses.
United States · Denmark · France - recruitingPHASE2
An Extension Study to Evaluate Safety and Efficacy of Atumelnant in Participants With Congenital Adrenal Hyperplasia
This study looks at the long-term safety and effectiveness of a new medicine, atumelnant, for people with Congenital Adrenal Hyperplasia (CAH). It's for those who have already tried atumelnant in a previous study and could benefit from continuing it.
United States · Argentina · Brazil - active not recruitingPHASE3
Global Safety and Efficacy Registration Study of Crinecerfont for Congenital Adrenal Hyperplasia
This study is testing a new medicine, crinecerfont, for adults with a condition called Congenital Adrenal Hyperplasia (CAH). It will compare crinecerfont to a dummy medicine to see if it's safe and helps manage CAH over about 20 months.
United States · Austria · Belgium - recruitingPHASE2
Pharmacokinetics, Safety and Tolerability of Crinecerfont in Participants With Congenital Adrenal Hyperplasia Who Are Less Than 2 Years Old
This study looks at a new medicine called crinecerfont for babies and toddlers under two years old with a condition called Congenital Adrenal Hyperplasia (CAH). Researchers want to see how the medicine works in their bodies and if it is safe.
Germany - active not recruitingPHASE3
Global Safety and Efficacy Registration Study of Crinecerfont in Pediatric Participants With Classic Congenital Adrenal Hyperplasia (CAHtalyst Pediatric Study)
This study is testing a new medicine, crinecerfont, for children and teenagers aged 2 to 17 with a type of Congenital Adrenal Hyperplasia (CAH). It compares the new medicine to a dummy pill (placebo) to see how well it works and if it's safe.
United States · Belgium · Canada - ongoing, recruitingTherapeutic exploratory (Phase II)
A 12-Week, Phase 2 Open-Label, Sequential Dose Cohort Study to Evaluate the Safety, Efficacy, and Pharmacokinetics of CRN04894 Treatment in Participants with Congenital Adrenal Hyperplasia
This study is looking at a new treatment called CRN04894 for people with Congenital Adrenal Hyperplasia (CAH). It will check if the treatment is safe, how well it works, and how the body handles it. This is an early-stage study.
Germany · Italy - not yet recruitingNA
Growing up With the Young Endocrine Support System (YESS!)
This study looks at a new game, YESS!, and a toolkit to help young people with long-term hormone conditions manage their health better as they move from children's to adult healthcare. The aim is to help them feel more in control and stick with their doctor's appointments.
Belgium · Netherlands · Spain - recruitingPHASE3
A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia
This study is testing a new medicine, atumelnant, for adults with a condition called congenital adrenal hyperplasia (CAH). It aims to see if the medicine is safe, works well, and how the body handles it.
United States · Argentina · Australia