Research.Patient.info
Cree Leukoencephalopathy research hub
2 indexed studies · 0 currently recruiting
- active not recruitingNA
Single Patient Investigational Treatment for Cree Leukoencephalopathy
This study is for a very rare, severe brain condition called Cree Leukoencephalopathy (CLE). There's no current cure. It tests a new drug called fosigotifator to see if it can slow down or stop the brain damage and improve a patient's health.
Canada - active not recruitingEARLY_PHASE1
Research Study for Single-Patient Treatment of Cree Leukoencephalopathy/Vanishing White Matter Disease
This study is looking at a new medicine called FGT for a very rare, serious brain condition called Cree Leukoencephalopathy (CLE), which is similar to Vanishing White Matter disease. It aims to see if FGT can help slow down the disease and improve life for a patient who currently has no other treatment options.
Canada