Erythropoietic Protoporphyria research hub

HELIOS: Open-Label, Long-Term Extension Study to Investigate the Safety, Tolerability, and Efficacy of DISC-1459 (Bitopertin) in Participants With EPP or XLP

This study looks at a new medicine called DISC-1459 (Bitopertin) for people with Erythropoietic Protoporphyria (EPP). It's an ongoing study to see if the medicine is safe, well-tolerated, and effective over a long time for those who have already tried it in earlier studies.