- recruitingPHASE3
A Study to Learn More About the Effects and Long-Term Safety of Omaveloxolone (BIIB141) in Children and Teens With Friedreich's Ataxia
This study looks at a medicine called omaveloxolone (SKYCLARYS®) for children and teenagers aged 2 to 15 with Friedreich’s Ataxia. It aims to see how well it works and if it's safe, as it's currently only approved for adults.
United States · Australia · Austria - recruiting
Patient-reported, Health Economic and Psychosocial Outcomes in Friedreich Ataxia
This study looks at how Friedreich Ataxia (FA) affects daily life for patients. It uses a mobile app to understand health, feelings, and costs over six months. The goal is to improve care and support for people with FA.
Austria · France · Germany - active not recruiting
FA Clinical Outcome Measures
This study looks into Friedreich's Ataxia (FA), a condition that affects the nervous system. It's helping researchers understand FA better and find new ways to measure its effects. While this specific study isn't taking new people, a similar updated study is now open for volunteers.
United States · Australia · Canada - active not recruitingPHASE3
A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia
This study looks at the long-term effects of a medicine called vatiquinone for people with Friedreich Ataxia. It's for those who have already taken part in a vatiquinone study, letting them continue treatment to see if it remains safe and helpful over time.
United States · Australia · Brazil - enrolling by invitationNA
The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period.
This study looks at how walking aids and training can help people with certain muscle and nerve conditions fall less often. It aims to improve their safety and daily life by finding the best ways to use these aids.
Germany - active not recruiting
A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA)
This study, called TRACK-FA, is looking at how Friedreich Ataxia (FA) affects the brain and spinal cord over two years. Researchers will use special scans and other tests to track changes in people with FA and compare them to healthy volunteers. This helps prepare for new FA treatments.
United States · Australia · Brazil - recruiting
Clinical Course Of Disease In Participants With FA-CM
This study looks at how a heart condition linked to Friedreich Ataxia (FA-CM) changes over time. It aims to understand how the heart gets worse and could lead to new gene therapy treatments in the future for people with FA-CM.
United States · Brazil · Canada - recruiting
Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
Researchers are studying Friedreich ataxia to better understand how the condition progresses and to help develop new treatments. This study will follow people with Friedreich ataxia for many years, gathering information about their health and how the condition affects them.
United States · Australia · Austria - not yet recruiting
Digital Outcome Assessment Using AI Active Gaming and Motion Capture in Friedreich Ataxia
This study uses AI and games to track movement in people with Friedreich Ataxia. It aims to find new, more accurate ways to measure disease changes for future treatment trials, making it easier and more relevant for patients.
United Kingdom