- recruitingPHASE1, PHASE2
A Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED)
This study is testing a new medicine, LY3884961, for adults with Gaucher disease, type 1. It aims to find the right dose and see how safe and effective it is for symptoms affecting the body, but not the brain.
United States · Australia · Brazil - recruiting
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
This study tracks the health of people with Gaucher disease over time, whether or not they are receiving treatment. There's also a sub-study for pregnant women with Gaucher disease to see how their pregnancies and babies' health progress. It helps doctors learn more about the condition.
United States · Argentina · Australia - recruiting
The GBA Multimodal Study in Parkinson's Disease
This study looks at how a specific gene change (GBA mutation) might be linked to Parkinson's disease. Researchers are using special brain scans and typing tests to understand changes in the brain and whether early signs of the disease can be found.
United States · Canada