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Generalised Lipodystrophy research hub
2 indexed studies · 1 currently recruiting
- recruiting
MEASuRE: Metreleptin Effectiveness And Safety Registry
This study, called MEASuRE, is tracking the long-term effects of a medicine called metreleptin for people with rare fat-wasting conditions called lipodystrophy. It's collecting real-world information to better understand how the medicine works and its safety outside of initial trials.
United States · France · Germany - ongoing, recruitingTherapeutic confirmatory (Phase III)
Open-label, Phase 3b study to evaluate effectiveness, safety and pharmacokinetic parameters of metreleptin in patients under 6 years of age with generalised lipodystrophy and associated diabetes mellitus and/or hypertriglyceridaemia
This study looks at a medicine called Myalepta for children under 6 with a rare condition called generalised lipodystrophy. We want to see how well it helps control blood sugar and fat levels, and if it's safe to use in these young children.
Italy · Germany · Belgium