Metilcrotonilglicinuria, biotinidasa deficit research hub

Development and delivery of personalized 3D-printed drugs to improve treatment adherence in children with rare diseases.

This study is exploring specially made 3D-printed medicines for children with rare conditions like methylcrotonylglycinuria and biotinidase deficiency. The aim is to see if these new medicines can help children take their treatment more easily and consistently, ultimately improving their health.