- active not recruitingPHASE2, PHASE3
A Study to Evaluate the Effect of Aficamten in Pediatric Patients With Symptomatic Obstructive Hypertrophic Cardiomyopathy (oHCM).
This study is looking into a new medicine called Aficamten for young people aged 12-17 with a heart condition called hypertrophic cardiomyopathy (oHCM). It aims to see if the medicine is safe and effective in improving their symptoms, compared to a dummy medicine.
United States · Canada · Italy - recruitingPHASE2
Efficacy of Rapamycin in the Treatment of Cervico-facial Lymphatic Malformations
This study looks at how well a medicine called rapamycin treats lymphatic malformations in children's faces and necks. Researchers want to see if it can shrink these growths, improve quality of life, and reduce bleeding over six months.
France - recruitingNA
Level Up! Adaptive Gaming for Children With Upper Limb Differences
This study looks at a special video game controller adapter for children aged 7-17 with one-sided arm or hand differences. It checks if the adapter helps them play games better and enjoy them more. Participants try the adapter at home and share their experiences.
Canada - active not recruitingPHASE3
Berotralstat Treatment in Children With Hereditary Angioedema
This study looks at a medicine called berotralstat for children aged 2 to 11 with hereditary angioedema (HAE). Researchers want to find the right dose for children based on their weight, check if it's safe, and see how well it prevents HAE attacks.
Austria · Canada · France - recruiting
Infant and Child European Cryoablation Project ICECaP
This study, called ICECaP, is gathering information about a freezing treatment called cryoablation for children with soft tissue problems. It aims to see how well it works, if it's safe, and what results different hospitals are getting.
United Kingdom