- recruitingTherapeutic exploratory (Phase II)
LONG-TERM INTERVENTIONAL FOLLOW-UP STUDY UP TO 4 YEARS OF AGE OF CHILDREN WITH PRADER-WILLI SYNDROME INCLUDED IN THE OTBB3 CLINICAL TRIAL AND COMPARISON WITH AN UNTREATED COHORT OF CHILDREN WITH PRADER-WILLI SYNDROME (OTBB3 FOLLOW-UP)
This study is looking at children with Prader-Willi Syndrome who took part in an earlier trial. Researchers want to see how they are doing up to four years later, especially regarding any health changes and how their previous treatment might have helped, compared to children who didn't receive that treatment.
France - recruitingTherapeutic exploratory (Phase II)
A Phase 2 Study to Evaluate Efficacy, Safety, and Pharmacokinetics of PBF-999 in the Treatment of Patients with Prader-Willi Syndrome.
This study is looking at a new medicine called PBF-999 for people with Prader-Willi Syndrome. We want to see if it's safe, how well it works, and how the body uses it. This is an early-stage study.
Spain - recruiting
Autistic Symptomatology and Sensory Profile in Children With Prader-Willi Syndrome
This study looks at how autism and sensory issues affect children with Prader-Willi Syndrome (PWS). Researchers want to understand these challenges better and see if early oxytocin treatment might make a difference, helping to improve care for these children.
France - active not recruitingPHASE3
Open-Label Extension Study of DCCR in Patients With Prader-Willi Syndrome
This study looks at the long-term safety of a medicine called DCCR for people with Prader-Willi syndrome. It's for those who have already taken part in a previous DCCR study.
United States · United Kingdom - recruitingPHASE3
A Study of Pitolisant in Patients With Prader-Willi Syndrome
This study is testing a medication called Pitolisant for people aged 6 and over with Prader-Willi syndrome. It aims to see if it helps with excessive sleepiness and other behaviors, compared to a dummy pill.
United States · Australia · Belgium