Research.Patient.info

Severe Combined Immunodeficiency (SCID) research hub

2 indexed studies · 2 currently recruiting

enrolling by invitation
Natural History Study of SCID Disorders
This study looks at how children with a rare immune problem called SCID respond to different treatments. Doctors are collecting information to understand which treatments work best and help these children live healthier lives. It's about naturally observing treatment journeys, not testing new drugs.
United States · Canada
enrolling by invitation
An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID
This study is checking on the long-term health of people who previously received a special gene therapy for a rare immune condition called ADA-SCID. It helps us understand how safe and effective the treatment is over many years. No new treatment is given in this study.
United States · United Kingdom