Research.Patient.info
X-Linked Chronic Granulomatous Disease research hub
2 indexed studies · 0 currently recruiting
- active not recruitingPHASE1, PHASE2
Study of EN-374 Gene Therapy in Participants With X-Linked Chronic Granulomatous Disease
This study is testing a new gene therapy called EN-374 for X-linked Chronic Granulomatous Disease (CGD). It aims to see if the treatment is safe and effective in helping the body fight off serious infections, looking initially at adults and then children.
United States · United Kingdom - recruitingPhase I/II
Study of EN-374 gene therapy in participants with X-linked chronic granulomatous disease
This study is testing a new gene therapy called EN-374 for X-linked chronic granulomatous disease (X-CGD). It aims to see if EN-374 is safe and effective in adults first, and then in children. We hope to improve the health of people with this rare immune condition.
United Kingdom · England · United States of America